A Phase 3, Double Blind, Randomized, Placebo-Controlled Trial to Evaluate the Efficacy and Safety of Setmelanotide in Patients With Acquired Hypothalamic Obesity

Status: Recruiting
Location: See all (5) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 3
SUMMARY

This is a sub-study of Study RM-493-040 (NCT05774756). The goal of this sub-study is to learn how well Setmelanotide works to improve weight reduction, hunger, and quality of life in patients 4 years of age and older with congenital Hypothalamic Obesity (cHO). To determine how well setmelanotide works and how safe it is, patients with cHO will take a daily injection of either setmelanotide or placebo and complete trial assessments for up to 26 weeks on a therapeutic regimen.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 4
Healthy Volunteers: f
View:

• Diagnosis of multiple pituitary hormone deficiency (MPHD), or septo-optic dysplasia (SOD), or optic nerve hypoplasia (ONH), or Childhood-onset combined pituitary hormone deficiency (CPHD), or Pituitary Stalk Interruption Syndrome (PSIS) with at least one pituitary deficiency AND a body mass index (BMI) of ≥30 kg/m2 for patients ≥18 years of age, or BMI ≥95th percentile for age and sex for patients 4 to \<18 years

• Age 4 years and older

• Weight gain associated with the hypothalamic injury and a BMI of ≥30 kg/m2 for patients ≥18 years of age or BMI ≥95th percentile for age and sex for patients 4 to \<18 years of age

• Agree to use a highly effective form of contraception throughout the study and for 90 days after the study

Locations
United States
Alabama
University of Alabama
RECRUITING
Birmingham
Massachusetts
Boston Children's Hospital
RECRUITING
Boston
Minnesota
Children's Minnesota
RECRUITING
Saint Paul
New York
Columbia University Irving Medical Center
RECRUITING
New York
Washington
Seattle Children's Research Institute
RECRUITING
Seattle
Contact Information
Primary
Rhythm Clinical Trials
clinicaltrials@rhythmtx.com
(857) 264-4280
Backup
Physician Inquiry Clinical Trials
clinicaltrials@rhythmtx.com
(857) 264-4280
Time Frame
Start Date: 2025-09-23
Estimated Completion Date: 2027-01-30
Participants
Target number of participants: 39
Treatments
Experimental: Setemelanotide
Randomized 2:1 (Setmelanotide: Placebo)
Placebo_comparator: Placebo
Randomized 2:1 (Setmelanotide: Placebo)
Sponsors
Leads: Rhythm Pharmaceuticals, Inc.

This content was sourced from clinicaltrials.gov

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