Latest Advances

  • Condition: Adenosine deaminase-deficient
  • Journal: Clinical immunology (Orlando, Fla.)
  • Treatment Used: Enzyme replacement therapy
  • Number of Patients: 1
  • Published —
The study researched an adenosine deaminase-deficient patient who used enzyme replacement therapy for 27 years.
  • Condition: Primary Immunodeficiency
  • Journal: Hematology. American Society of Hematology. Education Program
  • Treatment Used: Allogeneic Transplant and Gene Therapy
  • Number of Patients: 0
  • Published —
This article discusses treatment of primary immunodeficiency disorders with allogeneic hematopoietic cell transplantation (HCT) and gene therapy (GT).
  • Condition: Primary Immunodeficiency Disease (PID)
  • Journal: BMC pediatrics
  • Treatment Used: Allogeneic Hematopoietic Stem Cell Transplantation (allo-HSCT)
  • Number of Patients: 112
  • Published —
This study evaluated children with primary immunodeficiency disease (PID).
  • Condition: Ligase IV Deficiency
  • Journal: BMC pediatrics
  • Treatment Used: Allogeneic Hematopoietic Stem Cell Transplantation
  • Number of Patients: 2
  • Published —
The study researched the outcomes of allogeneic hematopoietic stem cell transplantation for patients with Ligase IV deficiency.
  • Condition: Children with Severe Combined Immunodeficiency (SCID)
  • Journal: Infectious diseases (London, England)
  • Treatment Used: Bacille Calmette-Guerin (BCG)
  • Number of Patients: 21
  • Published —
This study reported clinical and immunological characteristics of patients referred with severe combined immunodeficiency (SCID) who suffered from Bacille Calmette-Guerin (BCG) complications.
  • Condition: Infants with and without Leukemia or Malignant Conditions, or Non-Malignant Conditions
  • Journal: JAMA pediatrics
  • Treatment Used: Allogeneic Hematopoietic Cell Transplant
  • Number of Patients: 2498
  • Published —
This study analyzed survival trends and other outcomes among infants who undergo allogeneic hematopoietic cell transplant.
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