A Multi-center, Phase 1/2a, First-in-human (FIH) Study Investigating the Safety, Tolerability, and Efficacy of AMT-260 in Adults With Unilateral Refractory Mesial Temporal Lobe Epilepsy (MTLE) Administered Via Magnetic Resonance Imaging (MRI)-Guided Convection-enhanced Delivery (CED)

Status: Recruiting
Location: See all (18) locations...
Intervention Type: Genetic
Study Type: Interventional
Study Phase: Phase 1/Phase 2
SUMMARY

The main goals of this clinical study are to learn if AMT-260 is safe and tolerable and works to reduce the frequency of seizures in adults with unilateral mesial temporal lobe epilepsy (MTLE).

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Maximum Age: 75
Healthy Volunteers: f
View:

• Diagnosis of unilateral refractory MTLE

• History of seizures with an average of ≥ 2 documented focal impaired awareness seizures or focal to bilateral tonic-clonic seizures per 30-day period in the 3 months prior to screening.

• On a stable type and dose regimen of up to a maximum of 4 approved Anti Seizure Drugs for at least 6 months prior to screening.

• Confirmed unilateral hippocampal pathology and concordant unilateral seizure focus

• No evidence of focal neurocognitive dysfunction, inconsistent with disease pathology- related MRI and/or (18F)FDG-PET findings.

• Women of childbearing potential (WOCBP) and fertile male subjects must be willing and able to use highly effective methods of birth control consistently and correctly throughout the study.

• For WOCBP only: Negative pregnancy test.

Locations
United States
Alabama
University of Alabama at Birmingham
RECRUITING
Birmingham
Arizona
Mayo Clinic Arizona
RECRUITING
Phoenix
California
Stanford University
RECRUITING
Palo Alto
Florida
Mayo Clinic Florida
RECRUITING
Jacksonville
Kansas
Kansas University Medical Center
NOT_YET_RECRUITING
Kansas City
Massachusetts
Massachusetts General Hospital
RECRUITING
Boston
Maryland
Johns Hopkins School of Medicine
RECRUITING
Baltimore
Midatlantic Epilepsy and Sleep Center
RECRUITING
Bethesda
Michigan
Corewell Health
RECRUITING
Grand Rapids
New Hampshire
Dartmouth Hitchcock Medical Center
RECRUITING
Lebanon
New Jersey
Northeast Regional Epilepsy Group
RECRUITING
Hackensack
Robert Wood Johnson Hospital
RECRUITING
New Brunswick
Ohio
Cleveland Clinic
RECRUITING
Cleveland
Ohio State University
RECRUITING
Columbus
Pennsylvania
Hospital of the University of Pennsylvania
RECRUITING
Philadelphia
Allegheny Health Network
NOT_YET_RECRUITING
Pittsburgh
Texas
Baylor Scott & White Medical Center
RECRUITING
Austin
Wisconsin
Medical College of Wisconsin
NOT_YET_RECRUITING
Milwaukee
Contact Information
Primary
uniQure
medinfo@uniqure.com
1-866-520-1257
Time Frame
Start Date: 2024-06-12
Estimated Completion Date: 2031-12
Participants
Target number of participants: 12
Treatments
Experimental: AMT-260
Cohort 1: AMT-260 starting dose (1.0x 10E12 gc/mL). Cohort 2: AMT-260 adapted dose (6.0x 10E11 gc/mL or 3.0x 10E12 gc/mL).
Related Therapeutic Areas
Sponsors
Leads: UniQure Biopharma B.V.

This content was sourced from clinicaltrials.gov