Spinal Muscular Atrophy Type 3Symptoms, Doctors, Treatments, Advances & More
Learn About Spinal Muscular Atrophy Type 3
Vanderbilt Medical Group- Teleneurology
. Dr. Lee is rated as a Distinguished provider by MediFind in the treatment of Spinal Muscular Atrophy Type 3. His top areas of expertise are Myasthenia Gravis, Amyotrophic Lateral Sclerosis (ALS or Lou Gehrig's Disease), Spinal Muscular Atrophy (SMA), Guillain-Barre Syndrome, and Gamma Knife Radiosurgery.
Reading Hospital
. Dr. Khoshnoodi is rated as an Advanced provider by MediFind in the treatment of Spinal Muscular Atrophy Type 3. His top areas of expertise are Peripheral Neuropathy, Guillain-Barre Syndrome, Chronic Polyradiculoneuritis, and Miller-Fisher Syndrome.
St. Jude Children's Research Hospital
Richard Finkel is a Pediatrics provider in Memphis, Tennessee. Dr. Finkel is rated as an Elite provider by MediFind in the treatment of Spinal Muscular Atrophy Type 3. His top areas of expertise are Spinal Muscular Atrophy (SMA), Primary Lateral Sclerosis, Spinal Muscular Atrophy Type 3, and Spinal Muscular Atrophy Type 2.
Summary: The objective of this study is to understand how spatiotemporal and kinetic gait parameters are associated with bone health in pwSMA who are receiving DMT. We hypothesize that gait parameters are associated with BMD and can determine fracture risk in pwSMA. This is an observational study that involves one in-clinic visit (approximately 3 hours) with remote follow-up visits (approximately 15 minute...
Summary: This double-blind, Phase 2, multiple-dose study will be conducted to evaluate the PK/PD, efficacy, safety, and tolerability of apitegromab in subjects \<2 years old with 5q autosomal recessive SMA who have delayed motor milestones for their age attributed to SMA at the discretion of the Investigator or a Children's Hospital of Philadelphia Infant Test of Neuromuscular Disorders (CHOP-INTEND) score...