Tubular Aggregate Myopathy
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Tubular Aggregate Myopathy Overview

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Learn About Tubular Aggregate Myopathy

Condition 101 content is not available at this time, but we are continually updating the site. Please check back.

However, there may be experts who have treated this or similar conditions in our Find a Doctor section and research may be available in our Latest Advances section.

Who are the top Tubular Aggregate Myopathy Local Doctors?
Elite in Tubular Aggregate Myopathy
Elite in Tubular Aggregate Myopathy

Penn Neuroscience Center - Neurology

3400 Civic Center Boulevard, South Pavilion, 2nd Floor, 
Philadelphia, PA 
Languages Spoken:
English
Accepting New Patients

James Dowling is a Neurologist practicing medicine in Philadelphia, Pennsylvania. Dr. Dowling is rated as an Elite provider by MediFind in the treatment of Tubular Aggregate Myopathy. He is also highly rated in 20 other conditions, according to our data. His clinical expertise encompasses Tubular Aggregate Myopathy, Congenital Fiber-Type Disproportion, X-Linked Myotubular Myopathy, and Horizontal Gaze Palsy with Progressive Scoliosis. Dr. Dowling is board certified in Neurology - Child Neurology, 2007. Dr. Dowling is currently accepting new patients.

Elite in Tubular Aggregate Myopathy
Elite in Tubular Aggregate Myopathy
Illkirch-graffenstaden, FR 

Johann Bohm practices practicing medicine in Illkirch-graffenstaden, France. Bohm is rated as an Elite expert by MediFind in the treatment of Tubular Aggregate Myopathy. They are also highly rated in 13 other conditions, according to our data. Their clinical expertise encompasses Tubular Aggregate Myopathy, X-Linked Myotubular Myopathy, Congenital Fiber-Type Disproportion, and Stormorken Syndrome.

 
 
 
 
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Elite in Tubular Aggregate Myopathy
Elite in Tubular Aggregate Myopathy
Illkirch-graffenstaden, FR 

Jocelyn Laporte practices practicing medicine in Illkirch-graffenstaden, France. Ms. Laporte is rated as an Elite expert by MediFind in the treatment of Tubular Aggregate Myopathy. She is also highly rated in 16 other conditions, according to our data. Her clinical expertise encompasses Tubular Aggregate Myopathy, X-Linked Myotubular Myopathy, Congenital Fiber-Type Disproportion, and Centronuclear Myopathy.

What are the latest Tubular Aggregate Myopathy Clinical Trials?
A Phase 1/2, Multicenter, Open-label, Dose Escalation and Expansion Clinical Study to Evaluate the Safety, Tolerability and Preliminary Efficacy of ASP2957 in Male Participants With Invasive Ventilator-dependent X-linked Myotubular Myopathy

Summary: X-linked myotubular myopathy (XLMTM) is a rare and serious condition present at birth where the muscles do not work properly. There are currently no approved therapies for XLMTM. The protein myotubularin is needed for muscle development, movement and breathing. A gene called MTM1 tells the body to make myotubularin. XLMTM is caused by changes, or mutations, in the MTM1 gene. Changes in the MTM1 ge...

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A Non-interventional, Epidemiologic Study of XLMTM and Clinical Expression in the Liver

Summary: XLMTM (X-linked myotubular myopathy) is a serious genetic muscle condition. It is caused by changes in the MTM1 gene which stops or slows down normal muscle development, causing severe muscle weakness. There is currently no cure for XLMTM. Ongoing care is needed to manage symptoms and prevent further medical problems from this condition. Recent research shows that individuals with XLMTM often have...