An Open-Label Uncontrolled Multicenter Study to Evaluate the Pharmacokinetics, Pharmacodynamics, Safety and Activity of Nipocalimab in Children Aged 2 to Less Than 18 Years With Generalized Myasthenia Gravis

Who is this study for? Children aged 2 to less than 18 years with generalized myasthenia gravis
What treatments are being studied? Nipocalimab
Status: Recruiting
Location: See all (19) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 2/Phase 3
SUMMARY

The purpose of this study is to determine the effect of nipocalimab on total serum immunoglobulin G (IgG) in pediatric participants 2 to less than (\<) 18 years of age (globally) and 8 to \<18 years of age (for Unites Stated (US) sites only), the safety and tolerability of treatment with nipocalimab in children and adolescents and to evaluate the pharmacokinetics (PK) of nipocalimab in children and adolescents with generalized myasthenia gravis (gMG) who have an insufficient clinical response to ongoing, stable standard-of-care therapy.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 2
Maximum Age: 17
Healthy Volunteers: f
View:

• Age: For US sites only: 8 to \< 18 years

• Diagnosis of myasthenia gravis (MG) with generalized muscle weakness meeting the clinical criteria for generalized myasthenia gravis (gMG) as defined by the Myasthenia Gravis Foundation of America (MGFA) Clinical Classification Class IIa/b, IIIa/b, or IVa/b at screening

• Has a positive serologic test for acetylcholine receptor (anti-AChR) antibodies or muscle-specific tyrosine kinase (anti-MuSK) antibodies at screening

• A participant using herbal, naturopathic, traditional Chinese remedies, ayurvedic or nutritional supplements, or medical marijuana (with a doctor's prescription) is eligible if the use of these medications is acceptable to the Investigator. These remedies must remain at a stable dose and regimen throughout the study

• Has sufficient venous access to allow drug administration by infusion and blood sampling as per the protocol

• Participants should have a body weight and body mass index between 5th and 95th percentile for age and sex. Obese participants greater than 95th percentile and underweight participants below 5th percentile may participate following medical clearance

• A female of childbearing potential must have a negative highly sensitive serum (beta-human chorionic gonadotropin \[beta-hCG\]) at Screening and a negative urine pregnancy test at Day 1 prior to administration of study intervention

Locations
United States
Arizona
Phoenix Children's Hospital
RECRUITING
Phoenix
California
Childrens Hospital Los Angeles
RECRUITING
Los Angeles
Lucile Packard Children's Hospital Stanford
RECRUITING
Palo Alto
UCSF Benioff Children's Hospital
RECRUITING
San Francisco
Colorado
Children's Hospital Colorado
RECRUITING
Aurora
Florida
University of South Florida Morsani Center for Advanced Healthcare
RECRUITING
Tampa
Kansas
University of Kansas Medical Center
COMPLETED
Lawrence
Michigan
C.S. Mott Children's Hospital
RECRUITING
Ann Arbor
Pennsylvania
Penn State Milton S Hershey Medical Ctr
RECRUITING
Hershey
Childrens Hospital Of Philadelphia
RECRUITING
Philadelphia
University of Pittsburgh Medical Center
TERMINATED
Pittsburgh
Other Locations
Japan
Nagano Children's Hospital
RECRUITING
Azumino-shi
Chiba University Hospital
RECRUITING
Chiba
University of Miyazaki Hospital
RECRUITING
Miyazaki
Hyogo College of Medicine Hospital
RECRUITING
Nishinomiya-shi
Saitama Prefecture Children's Medical Center
RECRUITING
Saitama Shi
Tokyo Women's Medical University Hospital
RECRUITING
Shinjuku-ku
Netherlands
Leiden University Medical Center
RECRUITING
Leiden
Poland
Uniwersyteckie Centrum Kliniczne
RECRUITING
Gdansk
Contact Information
Primary
Study Contact
Participate-In-This-Study1@its.jnj.com
844-434-4210
Time Frame
Start Date: 2022-07-20
Estimated Completion Date: 2026-06-26
Participants
Target number of participants: 12
Treatments
Experimental: Nipocalimab
Participants age 2 to less than (\<) 18 years of age (globally) and 8 to \<18 years of age (for US sites only) will be divided into 2 cohorts as per their age-adolescents 12 to \<18 years and children 2 to \<12 years and will receive nipocalimab once every two weeks for 24 weeks. After Week 24, all participants will have the option to enroll in long term extension (LTE).
Related Therapeutic Areas
Sponsors
Leads: Janssen Research & Development, LLC

This content was sourced from clinicaltrials.gov

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