Tofersen
Last Updated: 02/24/2026
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Found 110 publications
Addendum to the 2023 clinical practice guidelines for amyotrophic lateral sclerosis in Japan: approval and integration of novel disease-modifying therapies.
Journal: Rinsho shinkeigaku = Clinical neurology
Published: January 21, 2026
Pharmacotherapy of neuromuscular diseases : what's new in 2025
Journal: Revue medicale suisse
Published: January 16, 2026
Tofersen, SOD1, and the Treatability of Amyotrophic Lateral Sclerosis.
Journal: JAMA neurology
Published: December 22, 2025
Facial-onset SOD1 amyotrophic lateral sclerosis: A case report and systematic review.
Journal: Journal of clinical neuroscience : official journal of the Neurosurgical Society of Australasia
Published: December 02, 2025
Amyotrophic lateral sclerosis in Saudi Arabia: a multicenter descriptive study.
Journal: Amyotrophic lateral sclerosis & frontotemporal degeneration
Published: November 24, 2025
Integrative treatment of the motor neuron disease amyotrophic lateral sclerosis, efficacy of pharmacotherapy, traditional Chinese medicine and importance of respiratory support, life-style, and gastrostomy-assisted nutrition: A review.
Journal: International journal of clinical pharmacology and therapeutics
Published: October 15, 2025
Real-world evidence supporting orphan drugs approvals for rare neuromuscular disorders in the European Union and the United States: Review of public assessment reports (2015-2025).
Journal: Current opinion in pharmacology
Published: October 08, 2025
Small RNA or oligonucleotide drugs and challenges in evaluating drug-drug interactions.
Journal: Frontiers in pharmacology
Published: October 07, 2025
Antisense Oligonucleotide Therapy for Amyotrophic Lateral Sclerosis (ALS): An Umbrella Review.
Journal: Cureus
Published: September 23, 2025
Disease-Modifying Therapies in Amyotrophic Lateral Sclerosis: A Network Meta-Analysis of Randomized Clinical Trials.
Journal: The Canadian journal of neurological sciences. Le journal canadien des sciences neurologiques
Published: September 19, 2025
Methotrexate therapy as a promising long-term treatment approach for immune-mediated adverse reactions of tofersen in SOD1-ALS: a case report.
Journal: Journal of neurology
Published: September 07, 2025
Targeting Amyotrophic Lateral Sclerosis with Gene Therapy: From Silencing Genes to Enhancing Neuroprotection.
Journal: Human gene therapy
Published: September 04, 2025
Last Updated: 02/24/2026