Tofersen
Last Updated: 06/30/2026
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Found 132 publications
Expanding the phenotypic spectrum of SOD1‑related ALS: upper motor neuron predominance in a p.D91A case.
Journal: Neurodegenerative disease management
Published: May 25, 2026
Bridging the Funding Gap in Drug Development for Amyotrophic Lateral Sclerosis.
Journal: Neurology. Clinical practice
Published: May 11, 2026
Fast and controlled access to tofersen for SOD1-related amyotrophic lateral sclerosis in The Netherlands; experiences using the orphan drug access protocol.
Journal: Amyotrophic lateral sclerosis & frontotemporal degeneration
Published: April 13, 2026
Longitudinal CSF and Serum Biomarker Dynamics in Tofersen-Treated SOD1-ALS: A Real-World Multicentre Cohort Study.
Journal: International journal of molecular sciences
Published: April 08, 2026
Longitudinal Analysis of Superoxide Dismutase 1 Seeding Activity in Amyotrophic Lateral Sclerosis Cerebrospinal Fluid.
Journal: medRxiv : the preprint server for health sciences
Published: April 03, 2026
Safety evaluation of Tofersen in amyotrophic lateral sclerosis based on the FAERS database.
Journal: Frontiers in neurology
Published: March 31, 2026
Tofersen in SOD1-associated amyotrophic lateral sclerosis: From molecular mechanisms to regulatory milestones.
Journal: European journal of pharmaceutical sciences : official journal of the European Federation for Pharmaceutical Sciences
Published: March 23, 2026
Tofersen treatment in SOD1 p.Leu145Phe ALS: real-world outcomes in a genetically homogeneous Croatian cohort.
Journal: Amyotrophic lateral sclerosis & frontotemporal degeneration
Published: March 13, 2026
Optimizing Research Operations and Resource Utilization in ALS Care: Insights From the Tofersen Antisense Oligonucleotide Expanded Access Protocol.
Journal: Muscle & nerve
Published: February 12, 2026
Long-Term Tofersen in SOD1 Amyotrophic Lateral Sclerosis.
Journal: JAMA neurology
Published: February 09, 2026
Tofersen: A Novel Option for the Treatment of Amyotrophic Lateral Sclerosis.
Journal: The Annals of pharmacotherapy
Published: February 05, 2026
Last Updated: 06/30/2026