A Randomized, Placebo-controlled Phase 2 Study to Demonstrate the Safety and Efficacy of the Addition of LAM-001 to Standard Immunosuppression Therapy for Chronic Lung Allograft Dysfunction (BOS).

Status: Recruiting
Location: See location...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 2
SUMMARY

The goal of this clinical trial is to learn about the safety and effectiveness of LAM-001 in patients who have developed bronchiolitis obliterans syndrome (BOS), a form of chronic rejection, after lung transplantation. The main questions it aims to answer are: * Is LAM-001 safe in these patients? * Is LAM-001 effective in slowing BOS progression? Participants will: * Be randomly assigned to inhale either LAM-001 or placebo (a look-alike substance that contains no active drug) daily for 48 weeks * Attend 10 study visits (mixture of in-person and telehealth) over the 48 week period * Undergo pulmonary function testing, bronchoscopy, lab testing, and physical examination * Submit weekly home spirometry monitoring Researchers will compare participants assigned to LAM-001 versus placebo to see if LAM-001 is safely tolerated and to assess the effectiveness of LAM-001 on slowing BOS progression.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Healthy Volunteers: f
View:

• Age \> 18 years old

• Recipient of a double pulmonary allograft at least 12 months before study entry

• Subjects with clinically diagnosed CLAD-BOS phenotype (all 3 required)

‣ BOS defined as screening FEV1 between 85-51% of the baseline as defined by the 2 highest FEV1 measures at least 3 weeks apart.

⁃ Diagnosis within 12 months of screening visit.

⁃ FEV1 decline is persistent as defined by decline sustained for \> 30 days.

• Currently receiving Standard Immunosuppression. This is defined as a combination of 3 medications including Prednisone, Mycophenolate or Azathioprine, and Tacrolimus or Cyclosporine. The dosing should be stable for 4 weeks prior to screening.

• Absence of oral sirolimus or everolimus treatment for at least 4 weeks prior to screening based on the half-life and resolution of the tissue effects

• Stable enough to enable routine post-transplant bronchoscopy with BAL and biopsy when indicated

• Capable of understanding the purposes and risks of the study

• Written informed consent (and assent when applicable) obtained from subject or subject's legal representative and ability for subject to comply with the requirements of the study.

• Women of childbearing potential must have a negative serum pregnancy test within 7 days prior to study entry

• Women of childbearing potential if sexually active must agree to using highly effective contraception during study and for 90 days after discontinuation of study treatment

• Women of childbearing potential must refrain from breast feeding or donating eggs for the duration of the study and for 90 days after the last dose of study treatment

• Male participants must agree to use a condom during sexual contact with a female of childbearing potential while participating in the study and for 90 days following discontinuation of investigational product use

• Male participants must refrain from donating sperm for the duration of the study and for 90 days after the last dose of study treatment

Locations
United States
California
University of California, San Francisco
RECRUITING
San Francisco
Contact Information
Primary
Steven Hays, MD
steven.hays@ucsf.edu
415-336-4141
Time Frame
Start Date: 2023-08-17
Estimated Completion Date: 2026-10
Participants
Target number of participants: 30
Treatments
Experimental: LAM-001
Placebo_comparator: Placebo
Sponsors
Collaborators: OrphAI Therapeutics
Leads: Steven Hays, MD

This content was sourced from clinicaltrials.gov

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