The Natural History of Arrhythmogenic Cardiomyopathy With Pathogenic Plakophilin-2 Variants (PKP2-ACM): An Observational Cohort Study

Status: Recruiting
Location: See all (3) locations...
Study Type: Observational
SUMMARY

The goal of this study is to describe the natural history and clinical events for patients who have Arrhythmogenic Cardiomyopathy with Pathogenic Plakophilin-2 Variants (PKP2-ACM) managed with standard of care.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 12
Healthy Volunteers: f
View:

⁃ Patients must meet all the following criteria (and none of the exclusion criteria) to be eligible for study participation:

• Male or female age 12 years or older at the time of providing informed consent (i.e., ICF provision).

• Capable and willing to provide signed informed consent and/or assent, which includes compliance with the requirements and restrictions listed in the ICF and protocol.

• Clinical diagnosis of arrhythmogenic cardio myopathy (ACM) as defined by the 2010 revised Task Force Criteria (TFC)

• Documentation of a pathogenic or likely pathogenic variant in PKP2 by a CLIA-certified genetic testing laboratory

• History of ICD implantation ≥6 months prior to ICF provision

• Left ventricular ejection fraction by echocardiogram or cardiac magnetic resonance (CMR) ≥50% at ≤12 months prior to ICF provision

Locations
United States
Massachusetts
Boston Children's Hospital
NOT_YET_RECRUITING
Boston
North Carolina
Duke University
RECRUITING
Durham
Other Locations
Netherlands
Amsterdam UMC
NOT_YET_RECRUITING
Amsterdam
Contact Information
Primary
Clinical Information
clinicaltrials@rocketpharma.com
646-627-0033
Time Frame
Start Date: 2025-09
Estimated Completion Date: 2028-12
Participants
Target number of participants: 36
Treatments
Prospective Cohort
Related Therapeutic Areas
Sponsors
Leads: Rocket Pharmaceuticals Inc.

This content was sourced from clinicaltrials.gov