CLN2 Disease Treatments
Find CLN2 Disease Treatments
Medications for CLN2 Disease
These are drugs that have been approved by the US Food and Drug Administration (FDA), meaning they have been determined to be safe and effective for use in CLN2 Disease.
Found 1 Approved Drug for CLN2 Disease
Brineura
Generic Name
Cerliponase
Brineura
Generic Name
Cerliponase
Form: Kit
FDA approval date: April 27, 2017
Brineura is indicated to slow the loss of ambulation in symptomatic pediatric patients 3 years of age and older with late infantile neuronal ceroid lipofuscinosis type 2 (CLN2), also known as tripeptidyl peptidase 1 (TPP1) deficiency. Brineura is a hydrolytic lysosomal N-terminal tripeptidyl peptidase indicated to slow the loss of ambulation in symptomatic pediatric patients 3 years of age and older with late infantile neuronal ceroid lipofuscinosis type 2 (CLN2), also known as tripeptidyl peptidase 1 (TPP1) deficiency. ( 1 )
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