A Pilot Study in the Treatment of Refractory Cytomegalovirus (CMV) Infections With Related Donor CMV Specific Cytotoxic T-cells (CTLs) in Children, Adolescents and Young Adult Recipients

Who is this study for? Patients with Cytomegalovirus Infections, Primary Immune Deficiency Disorder
What treatments are being studied? Viral Specific Cytotoxic T-Lymphocytes
Status: Recruiting
Location: See all (9) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 2
SUMMARY

CMV cytotoxic T cells (CTLs) manufactured with the Miltenyi CliniMACS Prodigy Cytokine Capture System will be administered in children, adolescents and young adults (CAYA) with refractory cytomegalovirus (CMV) infection post Allogeneic Hematopoietic Stem Cell Transplantation (AlloHSCT), with primary immunodeficiencies (PID) or post solid organ transplant. Funding Source: FDA OOPD

Eligibility
Participation Requirements
Sex: All
Minimum Age: 1 month
Maximum Age: 79
Healthy Volunteers: f
View:

‣ 1\. Patients with refractory CMV infection post allogeneic HSCT, with primary immunodeficiencies or post solid organ transplant with either

• Increasing or persistent quantitative qRT-PCR DNA copies despite two weeks of appropriate anti-viral therapy AND/OR

• Medical intolerance to anti-viral therapies including:

• ANC \< 500/mm2 secondary to ganciclovir

⁃ 2 renal toxicity with foscarnet And/or

• known resistance to ganciclovir and/or foscarnet

‣ Consent: Written informed consent given (by patient or legal representative) prior to any study-related procedures.

‣ Performance Status \> 30% (Lansky \< 16 yrs and Karnofsky \> 16 yrs) Age: 0.1 to 79.99 years Females of childbearing potential with a negative urine pregnancy test

‣ Donor Eligibility Related donor available with a T-cell response to the CMV MACS® GMP PepTivator antigen(s).

‣ a. Third Party Allogeneic Donor: If original donor is not available or does not have a T-cell response: third party related allogeneic donor (family donor \> 1 HLA A, B, DR match to recipient) with IgG positive to CMV and/or a T-cell response to the CMV MACS® GMP PepTivator .

‣ AND Allogeneic donor disease screening is complete similar to hematopoietic stem cell donors (Appendix 1).

‣ AND Obtained informed consents by donor or donor legally authorized representative prior to donor collection.

Locations
United States
California
Children's Hospital Los Angeles
RECRUITING
Los Angeles
University of California San Francisco
RECRUITING
San Francisco
Indiana
Indiana University
RECRUITING
Indianapolis
Maryland
Johns Hopkins
RECRUITING
Baltimore
Missouri
Washington University
RECRUITING
St Louis
New York
New York Medical College
RECRUITING
Valhalla
Ohio
Nationwide Children's Hosptial
RECRUITING
Columbus
Pennsylvania
Children's Hospital of Pennsylvania
RECRUITING
Philadelphia
Wisconsin
Medical College of Wisconsin/Children's Hospital of Wisconsin
RECRUITING
Milwaukee
Contact Information
Primary
Mitchell S Cairo, MD
mitchell_cairo@nymc.edu
914-594-2150
Backup
Lauren Harrison, RN
lauren_harrison@nymc.edu
6172857844
Time Frame
Start Date: 2018-11-01
Estimated Completion Date: 2027-12-31
Participants
Target number of participants: 20
Treatments
Experimental: Refractory CMV
Patients with refractory CMV will be given one dose of CMV specific CTLs. HLA matched donors will get Dose 2.5 × 10(4) CD3/kg recipient weight; HLA mismatched will get 0.5x10(4) CD3/kg recipient weight. Additional doses may be given for a total of 5 doses if patients do not have a response to the first dose with a reduction in viral load to normal limits.
Sponsors
Collaborators: Indiana University, Washington University School of Medicine, Nationwide Children's Hospital, Medical College of Wisconsin, Children's Hospital Los Angeles, Children's Hospital of Philadelphia, Johns Hopkins University, University of California, San Francisco
Leads: New York Medical College

This content was sourced from clinicaltrials.gov