Metastatic Ewing's Trial Testing Schedule Enhancement to Improve Outcomes

Status: Recruiting
Location: See all (17) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 1
SUMMARY

This single arm study is designed to demonstrate the feasibility of a radically different approach for an exceptionally high-risk subset of MES with widely metastatic disease (WMES). We incorporate the use of evolutionary principles that apply to species and population dynamics as related to adaptation and extinction to populations of cancer cells that similarly adapt and that we are attempting to make extinct, resulting in a cure for the patient. Such principles include an initial intense first strike to deplete the bulk of the cancer cells, followed by a series of sequential second strikes towards eliminating residual, resistant populations, followed by a prolonged period of maintenance chemotherapy to eliminate any remnant cells, using agents generally regarded to be active against newly diagnosed ES.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 1
Healthy Volunteers: f
View:

• Patients must be \>1 year of age. There is no upper age limit.

• Patients, in the opinion of the enrolling investigator, must be healthy enough to tolerate protocol therapy.

• Patients must have a new histologic diagnosis of either: widely metastatic Ewing sarcoma or metastatic CIC-rearranged sarcoma.

• Patients must have sufficient tissue submitted (flash frozen tissue, FFPE block, or up to 10 unstained FFPE slides) for correlative testing. This may be from a primary or metastatic site.

• Patients must not have received any prior systemic therapy with the exception that they may have started an initial cycle of vincristine/doxorubicin/cyclophosphamide (VDC) prior to enrollment, i.e. VDC may have been given, but not ifosfamide/etoposide (IE).

• Adequate organ function.

• Males and females of reproductive potential may not participate unless they have agreed to the use of, at minimum, two methods of contraception during and after treatment or abstinence.

• All patients and/or their parents or legal guardians must have the ability to understand and the willingness to sign a written informed consent or assent document.

Locations
United States
Alabama
University of Alabama at Birmingham (Children's of Alabama)
NOT_YET_RECRUITING
Birmingham
Arizona
Phoenix Children's Hospital
NOT_YET_RECRUITING
Phoenix
Connecticut
Connecticut Children's Medical Center
NOT_YET_RECRUITING
Hartford
Florida
University of Florida
NOT_YET_RECRUITING
Gainesville
Nemours Jacksonville
NOT_YET_RECRUITING
Jacksonville
University of Miami
NOT_YET_RECRUITING
Miami
Moffitt Cancer Center
RECRUITING
Tampa
Kentucky
University of Kentucky
NOT_YET_RECRUITING
Lexington
Michigan
Helen DeVos Children's Hospital
NOT_YET_RECRUITING
Grand Rapids
North Carolina
University of North Carolina
NOT_YET_RECRUITING
Chapel Hill
Levine Cancer Institute
NOT_YET_RECRUITING
Charlotte
New York
Roswell Park Comprehensive Cancer Center
NOT_YET_RECRUITING
Buffalo
Montefiore Medical Center
NOT_YET_RECRUITING
The Bronx
Ohio
Cleveland Clinic Children's
NOT_YET_RECRUITING
Cleveland
Nationwide Children's Hospital
NOT_YET_RECRUITING
Columbus
Tennessee
Vanderbilt University Medical Center
NOT_YET_RECRUITING
Nashville
Utah
Primary Children's Hospital
NOT_YET_RECRUITING
Salt Lake City
Contact Information
Primary
Jessica Crimella
Jessica.Crimella@moffitt.org
813-745-6250
Time Frame
Start Date: 2025-10
Estimated Completion Date: 2030-10
Participants
Target number of participants: 15
Treatments
Experimental: Sequential Therapy
Weeks 1-8, Vincristine/Doxorubicin/Cyclophosphamide. Weeks 9-14, Irinotecan, Ifosfamide, Vincristine, Actinomycin (IrIVA). Weeks 15-20, Cabozantinib w/ primary site radiation. Weeks 21-26, Topotecan/Cyclophosphamide. Weeks 27-32, High Dose Ifosfamide. Weeks 33-38, Irinotecan/Temozolomide. Maintenance, Weeks 39 up to 104, will consist of alternating 28-day blocks of chemotherapy (Block 1 and Block 2). Oral Cyclophosphamide / Oral Etoposide (Block 1). Vincristine/ Liposomal Doxorubicin (Block 2).
Sponsors
Leads: H. Lee Moffitt Cancer Center and Research Institute
Collaborators: National Pediatric Cancer Foundation

This content was sourced from clinicaltrials.gov