A Phase 4 Open-label Study to Evaluate the Safety After Switching to CSL312 (Garadacimab) From Current Prophylactic HAE Treatment in Subjects With HAE ≥ 12 Years of Age

Status: Recruiting
Location: See all (6) locations...
Intervention Type: Biological
Study Type: Interventional
Study Phase: Phase 4
SUMMARY

This study is designed to evaluate the safety after switching to garadacimab from another prophylactic hereditary angioedema (HAE) treatment (marketed kallikrein \[KK\] inhibitor or plasma-derived C1-esterase inhibitor \[pdC1INH\]prophylactic) when administered once monthly for approximately 3 months in participants aged greater than or equal to (\>=) 12 years with HAE.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 12
Healthy Volunteers: f
View:

• Aged \>= 12 years at the time of providing written informed consent / assent.

• Have a history of response to on-demand HAE treatment for the treatment of acute HAE attacks.

• Documented laboratory diagnosis in medical records of C1-esterase inhibitor hereditary angioedema (HAE-C1INH) type 1 or type 2:

‣ Documented clinical history consistent with HAE (subcutaneous or mucosal, nonpruritic swelling episodes without accompanying urticaria),

⁃ C1-esterase inhibitor (C1INH) antigen concentration or functional activity less than (\<) 50% of normal as documented in the participant's medical record, or

⁃ C4-antigen concentration below the lower limit of the reference range as documented in the participant's medical record.

∙ For HAE-nC1INH: Documented clinical history consistent with HAE (subcutaneous or mucosal, nonpruritic swelling episodes without accompanying urticaria); an HAE-associated FXII gene mutation (eg, FXII point mutation Thr328Lys or Thr328Arg, or deletion of 72 base pairs \[c.971\_1018 + 24del72\], or duplication of 18 base pairs \[c.892-909dup\]), as documented in the participant's medical record, OR an HAE-associated plasminogen gene mutation (PLG) gene mutation (eg, PLG point mutation Lys330Glu), as documented in the participant's medical record; C1INH antigen concentration or functional activity 70 to 120% of the normal level, as documented in the participant's medical record.

∙ • Use of lanadelumab, berotralstat, or pdC1INH for the prophylactic treatment of HAE and be on a stable (consistent) dose / regimen of such medication for at least 3 months prior to Screening.

Locations
United States
Arkansas
Allergy and Asthma Clinic of Northwest Arkansas
RECRUITING
Bentonville
Arizona
Research Solutions of Arizona
RECRUITING
Litchfield Park
California
Donald Levy M.D.
RECRUITING
Orange
Raffi Tachdjian MD, Inc.
RECRUITING
Santa Monica
Ohio
Bernstein Clinical Research Center, LLC
RECRUITING
Cincinnati
Other Locations
Canada
Clinique Spécialisée en Allergie de la Capitale
RECRUITING
Québec
Contact Information
Primary
Trial Registration Coordinator
clinicaltrials@cslbehring.com
+1 610-878-4697
Time Frame
Start Date: 2025-03-19
Estimated Completion Date: 2026-06-15
Participants
Target number of participants: 30
Treatments
Experimental: Garadacimab
Related Therapeutic Areas
Sponsors
Leads: CSL Behring

This content was sourced from clinicaltrials.gov