Phase I Dose Escalation and Preliminary Efficacy Study of Bispecific CD19 and CD22 Chimeric Antigen Receptor Co-Expressing T Cells (CD19x22 CAR T) in Pediatric Patients With Relapsed and/or Refractory B-Cell Acute Lymphoblastic Leukemia (B-ALL)

Status: Recruiting
Location: See location...
Intervention Type: Biological
Study Type: Interventional
Study Phase: Phase 1
SUMMARY

This study will evaluate the safety and tolerability of administering a novel bispecific CD19/CD22-directed CAR T cell product (CD19x22) for the treatment of relapsed or refractory pediatric B-ALL.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 3 months
Maximum Age: 30
Healthy Volunteers: f
View:

• Subjects must have a history of B precursor ALL with any of the following conditions:

‣ Relapsed two or more times.

⁃ Relapsed at any time after allogeneic bone marrow transplant (BMT).

⁃ Relapse or refractory after single antigen targeting CAR T cell therapy.

• i. 90 days must have elapsed post previous CAR infusion prior to apheresis. d. Refractory to standard therapy as determined by the treating physician. e. Patient and/or parents declining BMT options and would prefer CAR T Therapy.

• CD19 and/or CD22 present on last relapsed/refractory disease evaluation.

• Performance score (Lansky or Karnofsky ≥ 50%; or Eastern Cooperative Oncology Group (ECOG) must be ≤2).

• Meets criteria for potential leukapheresis collection or has leukapheresis product previously collected and stored per recommended guidelines.

• Males OR non-pregnant, non-lactating females.

• Aged 3 months to 30 years (inclusive) at time of consent and enrollment.

• Provision of a signed and dated consent form from parent or guardian (patients \< 18), the patient themselves (\> 18), or legally authorized representative (patient \> 18 who lack decision-making capacity) after standard of care (SOC) screening assessments are performed.

• Stated willingness to comply with all study procedures and be available for the duration of the study.

• Willingness to participate in long-term follow-up protocol.

Locations
United States
Colorado
Children's Hospital Colorado
RECRUITING
Aurora
Contact Information
Primary
Vanessa Fabrizio, MD
BMT@childrenscolorado.org
720-777-6860
Time Frame
Start Date: 2024-09-27
Estimated Completion Date: 2029-12
Participants
Target number of participants: 53
Treatments
Experimental: High Disease Burden Cohort
≥25% bone marrow lymphoblasts and/or non-CNS extramedullary disease. Dose escalation will proceed independently within each cohort using the Bayesian Optimal Interval (BOIN)design. Dose begins at DL -1(1x10\^5 cells/kg).
Experimental: Low Disease Burden Cohort
\<25% bone marrow lymphoblasts and no non-CNS extramedullary disease. Dose escalation will proceed independently within each cohort using the Bayesian Optimal Interval (BOIN)design. Dose begins at DL1 (3x10\^5 cells/kg).
Sponsors
Leads: University of Colorado, Denver

This content was sourced from clinicaltrials.gov

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