Latest Advances

  • Condition: Pantothenate Kinase-associated Neurodegeneration
  • Journal: Orphanet journal of rare diseases
  • Treatment Used: Pantethine
  • Number of Patients: 15
  • Published —
In this study, researchers evaluated the outcomes of using pantethine for the treatment of pantothenate kinase-associated neurodegeneration in children.
  • Condition: Pantothenate Kinase-Associated Neurodegeneration
  • Journal: The Lancet. Neurology
  • Treatment Used: Deferiprone
  • Number of Patients: 100
  • Published —
This study tested the safety and efficacy of using deferiprone to treat patients with pantothenate kinase-associated neurodegeneration.
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