LIGHTBEAM-U01 Substudy 01C: A Phase 1/2 Substudy to Evaluate the Safety and Efficacy of Patritumab Deruxtecan in Pediatric Participants With Relapsed or Refractory Solid Tumors

Status: Recruiting
Location: See all (22) locations...
Intervention Type: Biological
Study Type: Interventional
Study Phase: Phase 1/Phase 2
SUMMARY

Researchers are looking for new ways to treat children with hepatoblastoma or rhabdomyosarcoma (RMS) that has relapsed or is refractory: * Hepatoblastoma is a common liver cancer in babies and very young children * RMS is a cancer that starts in muscle cells, often in a child's head and neck, bladder, arms, or legs * Relapsed means the cancer came back after treatment * Refractory means the cancer did not respond (get smaller or go away) to treatment The study treatment HER3-DXd (also known as MK-1022 or patritumab deruxtecan) is an antibody-drug conjugate (ADC). An ADC attaches to a protein on cancer cells and delivers treatment to destroy those cells. The goals of this study are to learn: * About the safety of HER3-DXd in children and if they tolerate it * What happens to HER3-DXd in children's bodies over time * If children who receive HER3-DXd have the cancer get smaller or go away

Eligibility
Participation Requirements
Sex: All
Minimum Age: 1 month
Maximum Age: 17
Healthy Volunteers: f
View:

• Has one of the following histologically confirmed advanced or metastatic solid tumors: Rhabdomyosarcoma (RMS), or Hepatoblastoma

• Has progressed after at least 1 prior systemic treatment for RMS or hepatoblastoma and who has no satisfactory alternative treatment option (ie, is ineligible for other standard treatment regimens)

• Participants who have adverse events (AEs) due to previous anticancer therapies must have recovered to Grade ≤1 or baseline. Participants with endocrine-related AEs who are adequately treated with hormone replacement or participants who have Grade ≤2 neuropathy are eligible

• Hepatitis B surface antigen (HBsAg) positive participants are eligible if they have received hepatitis B virus (HBV) antiviral therapy and have undetectable HBV viral load

• Participants with a history of hepatitis C virus (HCV) infection are eligible if HCV viral load is undetectable

Locations
United States
Colorado
Children's Hospital Colorado-Center for Cancer and Blood Disorders ( Site 3016)
RECRUITING
Aurora
Iowa
University of Iowa Health Care Holden Comprehensive Cancer Center ( Site 3017)
RECRUITING
Iowa City
North Dakota
Sanford Fargo Medical Center-Roger Maris Cancer Center ( Site 3003)
RECRUITING
Fargo
New Jersey
Rutgers Cancer Institute of New Jersey ( Site 3008)
RECRUITING
New Brunswick
New York
New York Medical College ( Site 3023)
RECRUITING
Valhalla
Pennsylvania
Children's Hospital of Philadelphia (CHOP) ( Site 3021)
RECRUITING
Philadelphia
South Dakota
Sanford Children's Hospital ( Site 3015)
RECRUITING
Sioux Falls
Texas
University of Texas-MD Anderson Cancer Center ( Site 3007)
RECRUITING
Houston
Utah
Intermountain - Primary Children's Hospital ( Site 3014)
RECRUITING
Salt Lake City
Other Locations
Belgium
UZ Gent ( Site 3428)
RECRUITING
Ghent
France
Bordeaux University Hospital - Pellegrin ( Site 3105)
RECRUITING
Bordeaux
Centre Leon-Berard ( Site 3100)
RECRUITING
Lyon
Centre Hospitalier Universitaire de Nantes - Hôpital Femme-Enfant-Adolescent Chu De Nantes ( Site 3104)
RECRUITING
Nantes
Israel
Sheba Medical Center ( Site 3675)
RECRUITING
Ramat Gan
Republic of Korea
Asan Medical Center-Pediatrics - Pedicatric Oncology ( Site 3973)
RECRUITING
Seoul
Seoul National University Hospital-Pediatrics ( Site 3972)
RECRUITING
Seoul
Spain
Hospital Universitari Vall d''Hebron ( Site 3716)
RECRUITING
Barcelona
Hospital Sant Joan de Déu ( Site 3717)
RECRUITING
Esplugues De Llobregat
Hospital Infantil Universitario Nino Jesus ( Site 3715)
RECRUITING
Madrid
Sweden
Sahlgrenska Universitetssjukhuset. ( Site 3634)
RECRUITING
Gothenburg
Taiwan
National Taiwan University Hospital ( Site 3983)
RECRUITING
Taiwan
United Kingdom
Royal Victoria Infirmary ( Site 3348)
RECRUITING
Newcastle Upon Tyne
Contact Information
Primary
Toll Free Number
Trialsites@msd.com
1-888-577-8839
Time Frame
Start Date: 2025-05-26
Estimated Completion Date: 2030-12-30
Participants
Target number of participants: 50
Treatments
Experimental: Patritumab Deruxtecan
Participants receive patritumab deruxtecan via IV infusion on Day 1 of each 3-week cycle until discontinuation or progression.
Sponsors
Collaborators: Daiichi Sankyo
Leads: Merck Sharp & Dohme LLC

This content was sourced from clinicaltrials.gov

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