Natural History of SMA: Long Term Longitudinal Study and Development of a Registry
Status: Recruiting
Location: See all (5) locations...
Study Type: Observational
SUMMARY
This is an investigator initiated observational study with the aim to record several aspects of function, care and adverse events in a large cohort of SMA patients followed longitudinally by using a structured academic disease registry.
Eligibility
Participation Requirements
Sex: All
Healthy Volunteers: f
View:
• all patients
Locations
Other Locations
Italy
Istituto Gaslini
RECRUITING
Genova
Nemo Sud
RECRUITING
Messina
Centro Clinico nemo
RECRUITING
Milan
Ospedale Bambino gesu
RECRUITING
Rome
Policlinico gemelli
RECRUITING
Rome
Contact Information
Primary
Eugenio Mercuri, MD
eugeniomaria.mercuri@policlinicogemelli.it
06 3015
Backup
Marika Pane, MD
marika.pane@policlinicogemelli.it
063015
Time Frame
Start Date: 2018-06-21
Estimated Completion Date: 2033-12-30
Participants
Target number of participants: 1200
Related Therapeutic Areas
Sponsors
Collaborators: University of Milan, Ospedale Pediatrico Bambin Gesù, Istituto Giannina Gaslini, University of Messina
Leads: Fondazione Policlinico Universitario Agostino Gemelli IRCCS