International Prospective Registry of Patients With Alpha Thalassemia
Status: Recruiting
Location: See location...
Study Type: Observational
SUMMARY
This is an international prospective registry of patients with Alpha thalassemia to understand the natural history of the disease and the outcomes of fetal therapies, with the overall goal of improving the prenatal management of patients with Alpha thalassemia.
Eligibility
Participation Requirements
Sex: All
Healthy Volunteers: f
View:
• diagnosis of alpha thalassemia (prenatal or postnatal) with genotype consistent with ATM or BHFS phenotype
• referred to the University of California, San Francisco Fetal Treatment Center for fetal diagnosis, management and/or evaluation for the ongoing in utero stem cell transplantation clinical trial
Locations
United States
California
University of California San Francisco
RECRUITING
San Francisco
Contact Information
Primary
Billie Lianoglou, LCGC
billie.lianoglou@ucsf.edu
(415) 476-2461
Time Frame
Start Date: 2017-01
Estimated Completion Date: 2037-01
Participants
Target number of participants: 500
Related Therapeutic Areas
Sponsors
Leads: University of California, San Francisco