Phase 1/2 Study: CD45RA Depleted Peripheral Stem Cell Addback to Prevent Viral and Fungal Infections Following Alternative Donor TCRab/CD19 Depleted Hematopoietic Stem Cell Transplant

Status: Recruiting
Location: See location...
Intervention Type: Device
Study Type: Interventional
Study Phase: Phase 1/Phase 2
SUMMARY

The major morbidities of allogeneic hematopoietic stem cell transplant (HSCT) using donors that are not human leukocyte antigen (HLA) matched siblings are graft vs host disease (GVHD) and life- threatening infections. T cell receptor alpha beta (TCRαβ) T lymphocyte depletion and CD19+ B lymphocyte depletion of alternative donor hematopoietic stem cell (HSC) grafts is effective in preventing GVHD, but immune reconstitution may be delayed, increasing the risk of infections. The central hypothesis of this study is that an addback of CD45RO memory T lymphocytes, derived from a fraction of the original donor peripheral stem cell product depleted of CD45RA naïve T lymphocytes, will accelerate immune reconstitution and help decrease the risk of infections in TCRab/CD19 depleted PSCT.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 1 month
Maximum Age: 25
Healthy Volunteers: f
View:

• Disease for which allogeneic HSCT may be curative.

• Remission status of hematologic malignancies and additional disease-specific eligibility determinations will be according to standards of practice within the CHOP Cellular Immunotherapy and Transplant Program (CTTS).

• Patients must be 25 years of age and less

• Evaluation for organ and infectious status as per our CTTS standard operating procedure.

• Signed consent by parent/guardian or able to give consent if 18 years of age and older.

• Participants of childbearing potential must have a negative pregnancy test as per institutional SOP.

Locations
United States
Pennsylvania
Children's Hospital of Philadelphia
RECRUITING
Philadelphia
Contact Information
Primary
Megan Atkinson
cttsbmtintake@chop.edu
215-590-2820
Backup
Linda Zitkus, BSN,RN
zitkusl@chop.edu
Time Frame
Start Date: 2025-03-21
Estimated Completion Date: 2032-03
Participants
Target number of participants: 100
Treatments
Experimental: Phase 1:TCRab/CD19 depleted PSCT with CD45RA depleted addback using mismatched related donors (MMRD)
Stem cell source: mobilized peripheral blood stem cells (PBSC)~Donor type: \> or = 5/10 mismatched related donor~Conditioning: disease specific standard of care (SOC) regimens
Experimental: Phase 2:TCRab/CD19 depleted PSCT with CD45RA depleted addback at MTD found in phase 1 using MMRD
Stem cell source: mobilized PBSC~Donor type: \> or = 5/10 mismatched related donor~Conditioning: disease specific SOC regimens
Experimental: Phase 2:TCRab/CD19 depleted PSCT with CD45RA depleted addback using unrelated donors
Stem cell source: mobilized PBSC~Donor type: 9/10 or 10/10 matched unrelated donor~Conditioning: disease specific SOC regimens
Sponsors
Leads: Children's Hospital of Philadelphia

This content was sourced from clinicaltrials.gov