Advanced in Maple Syrup Urine Disease

Marina Cavazzana

Paris, FR 
Advanced in Maple Syrup Urine Disease
Paris, FR 
OverviewLocationsClinical Research

Overview

Marina Cavazzana practices in Paris, France. Ms. Cavazzana is rated as an Advanced expert by MediFind in the treatment of Maple Syrup Urine Disease. Her top areas of expertise are Hemoglobinopathy, Sickle Cell Disease, Congenital Hemolytic Anemia, Bone Marrow Transplant, and Bone Graft.

Her clinical research consists of co-authoring 162 peer reviewed articles and participating in 1 clinical trial. MediFind looks at clinical research from the past 15 years. In particular, she has co-authored 2 articles in the study of Maple Syrup Urine Disease.

Gender
Female

Locations

Paris, France
Other Locations
Colombes, France

Clinical Research

Clinical research consists of overseeing clinical studies of patients undergoing new treatments and therapies, and publishing articles in peer reviewed medical journals. Experts who actively participate in clinical research are generally at the forefront of the fields and aware of the most up-to-date advances in treatments for their patients.

1 Clinical Trials

Long Term Safety Follow up of Patients Enrolled in the Phase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome (GTG002-07 and GTG003-08).
Long Term Safety Follow up of Patients Enrolled in the Phase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome (GTG002-07 and GTG003-08).
Enrollment Status: Active_not_recruiting
Publish Date: June 03, 2021
Intervention Type: Genetic
Study Drug: Autologous CD34-Positive WASP Lentiviral Vector-Transduced Cells
Study Phase: Phase 1/Phase 2

161 Total Publications

Securing raw materials, reagents, and consumable supplies in the academic bioproduction UNITC network: because the chain is only as strong as its weakest link.
Securing raw materials, reagents, and consumable supplies in the academic bioproduction UNITC network: because the chain is only as strong as its weakest link.
Journal: Bone marrow transplantation
Published: July 30, 2025

Areas of Expertise

MediFind evaluates expertise by pulling from factors such as number of articles a doctor has published in medical journals, participation in clinical trials, speaking at industry conferences, prescribing and referral patterns, and strength of connections with other experts in their field.

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